A compact Cas12f nuclease shows high editing efficiency in human cells, with structural insights enabling an engineered variant potentially suited for future AAV‑compatible delivery.
A research team has discovered an enhanced CRISPR gene-editing system that could enable targeted delivery inside the human ...
By Nancy Lapid April 17 (Reuters) - Researchers have developed a modified version of the CRISPR gene-editing tool that in ...
The ACC has published a scientific statement regarding the use of gene editing therapy for cardiovascular disease.
This guidance emphasises the potential of NGS methods in mitigating safety risks associated with therapies incorporating ...
Scientists have corrected an extremely rare and life-threatening genetic disease of the liver in mouse models and human ...
In a new study published in Genes & Development, research led by Dr. Lila Allou at the MRC Laboratory of Medical Sciences ...
The US Food and Drug Administration (FDA) has released draft guidance on how sponsors can utilize next-generation sequencing ...
In 2025, baby KJ Muldoon became the first person to receive a personalized gene editing treatment, which likely saved his ...
Gene‑edited HPSCs programmed to make therapeutic antibodies and proteins show long‑lasting, boostable immunity in mouse models.
Researchers used CRISPR to edit hematopoietic stem cells, creating B cells that produce neutralizing antibodies against HIV, ...
For the millions of people living with genetic diseases like muscular dystrophy and inherited liver disorders, one of the ...